Daniel Cressy's illness was a barrier to getting his pilot's license, until a novel treatment was approved in the United ...

Gene editing has delivered remarkable results against sickle cell disease. Now researchers are working to make these personalized treatments faster, cheaper, and available to far more patients.

Daniel Cressy, 23, says path leading to completion of curative gene therapy is his ‘greatest blessing’ ...

Sickle cell is a genetic blood condition that can cause severe pain, extreme tiredness and serious health complications. It mainly affects people of African and Caribbean heritage, and for many, it's ...

The first person to ever be cured of sickle cell anemia in Louisiana received revolutionary gene therapy. The treatment is now offered at this hospital.

After living with the most severe form of sickle cell disease for 17 years, a Knoxville teen is undergoing a groundbreaking ...

Learn how gene editing is transforming sickle cell disease treatment and why expanding access to younger children matters.

Jason is a general assignment reporter, with particular focus on genetic medicine and rare disease. Confidential tips can be sent on Signal at JasonMast.77. Fulcrum Therapeutics said Sunday that a ...

Add Yahoo as a preferred source to see more of our stories on Google. Sickle cell disease reshapes healthy round blood cells into a sickled C-shape. As these sticky cells clump up, they can block ...

A Knoxville teenager traveled to Nashville to receive a new form of gene therapy treatment for his sickle cell disease.

Serenity Cole enjoyed Christmas last month relaxing with her family near her St. Louis home, making crafts and visiting friends. It was a contrast to how Cole, 18, spent part of the 2024 holiday ...

Agios Pharmaceuticals shares rose Tuesday after the U.S. Food and Drug Administration granted priority review to the company's supplemental new drug application for mitapivat to treat sickle cell ...